CGTLive

PROPEL is evaluating a lower dose and a higher dose of PR001 in 2 separate cohorts. #Parkinsons #ParkinsonsDisease #ClinicalTrialsInProgress Prevail Therapeutics Eli Lilly and Company Read more: https://lnkd.in/ezYappQP

ICYMI: We're excited to introduce the #ImmunoLogic video podcast, hosted by Joseph Fraietta, PhD, an assistant professor of microbiology and the director of the Fraietta Lab at the University of Pennsylvania (Penn Medicine, University of Pennsylvania Health System)! #celltherapy #genetherapy Watch now: https://lnkd.in/eXrtvxca

It was determined that for an accelerated approval the composite Unified Huntington’s Disease Rating Scale (cUHDRS) may constitute an intermediate clinical end point. #HuntingtonsDisease #HuntingtonDisease #genetherapy uniQure Read more: https://lnkd.in/gHj_pMx8

ICYMI: Yesterday the FDA approved Mesoblast Limited's Ryoncil (remestemcel-L-rknd), an allogeneic bone marrow-derived mesenchymal stromal cell therapy, for the treatment of steroid-refractory acute graft-versus-host disease in pediatric patients aged 2 months or older. #FDAapproval #FDAnews #celltherapy

From tackling #AutoimmuneDiseases and #fibrosis to offering new hope for conditions such as #Alzheimers and #Parkinsons, #NKcells are proving to be more versatile—and more promising—than ever before. Read more: https://lnkd.in/eRnswPh9

PepGen pointed out that it has not yet received an official clinical hold letter from the FDA, but that the agency stated the letter will be provided within 30 days. #Duchenne #MuscularDystrophy #ExonSkipping @PepGenTx Read more: https://lnkd.in/e3jkN-Ej

The FDA has approved Mesoblast Limited's Ryoncil (remestemcel-L-rknd), an allogeneic bone marrow-derived mesenchymal stromal cell therapy, for the treatment of steroid-refractory acute graft-versus-host disease in pediatric patients aged 2 months older. #FDAapproval #FDAnews #celltherapy

We're excited to introduce the #ImmunoLogic video podcast, hosted by Joseph Fraietta, PhD, an assistant professor of microbiology and the director of the Fraietta Lab at the University of Pennsylvania (Penn Medicine, University of Pennsylvania Health System)! #celltherapy #genetherapy Watch now: https://lnkd.in/eXrtvxca

• Roche Dumps Phase 3 Trial for #HemophiliaA Gene Therapy SPK-8011 • GenSight Biologics in Troubled Financial Straits Have a #celltherapy or #genetherapy update you’d like to share? Tag us with #AroundTheHelix! https://lnkd.in/ecRHsCif

In Mind Moments®, a podcast from our sister site NeurologyLive®, Jonathan Parker, MD, PhD (Mayo Clinic) spoke on the emerging interest in #celltherapy as a potential means to address #epilepsy. Listen now: https://lnkd.in/enaf6KFA